Ultragenyx Pharmaceutical
RAREUltragenyx Pharmaceutical is a biopharmaceutical company focused on the development and commercialization of novel therapies for serious rare and ultra-rare genetic diseases.
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Aug 4, 2026 (In 6 days)Valuation & ratios
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Profile
Ultragenyx Pharmaceutical is a biopharmaceutical company focused on the development and commercialization of novel therapies for serious rare and ultra-rare genetic diseases. The company leverages a diverse portfolio of biologics, small molecules, and gene therapies to address conditions with high unmet medical needs and well-understood biology. Its value proposition is built on an integrated model of in-licensing promising candidates and maintaining global commercialization rights through a specialized, patient-focused organization.
A leading developer in the ultra-rare disease space with a first-in-class portfolio and a robust gene therapy manufacturing infrastructure.
Questions, answered.
- What is Ultragenyx Pharmaceutical's market cap?
- Ultragenyx Pharmaceutical (RARE) has a market capitalization of $2.6B and trades on NASDAQ.
- What is Ultragenyx Pharmaceutical's revenue and profitability?
- Ultragenyx Pharmaceutical generated $669.7M in trailing twelve-month revenue with a net loss of $608.9M, representing a net margin of -90.9%. Gross margin stands at 97.2%, with free cash flow of -$503.0M. These figures are based on the Q1 2026 filing.
- Who are Ultragenyx Pharmaceutical's competitors?
- Ultragenyx Pharmaceutical's key competitors include Arrowhead Pharmaceuticals, Amgen, Ionis Pharmaceuticals, and others. These companies compete in similar markets and product categories.
- Who does Ultragenyx Pharmaceutical partner with?
- Ultragenyx Pharmaceutical's notable partners include Kyowa Kirin Co., Ltd., Regeneron Pharmaceuticals, Mereo BioPharma, and others.
- What subsidiaries does Ultragenyx Pharmaceutical have?
- Ultragenyx Pharmaceutical's subsidiaries include GeneTx Biotherapeutics LLC.
- Where is Ultragenyx Pharmaceutical headquartered?
- Ultragenyx Pharmaceutical is headquartered in United States of America and employs approximately 1,276 people. It has been publicly traded since 2014.
